Conference Day One

Wednesday 15th March 2023

8:00 am Registration & Welcome Coffee

8:25 am Chair’s Opening Remarks

  • Kirk Tanner CSO and SVP Brain Tumor Investment Fund, National Brain Tumor Society

Reviewing Glioblastoma Clinical Updates in the Past Year: The Successes & Failures

8:30 am Examining the Current Landscape of Glioblastoma Therapies & Strategies to Improve Outcomes

  • Patrick Wen Director - Center For Neuro-Oncology, Dana-Farber Cancer Institute

Synopsis

  • Overview of novel therapies for GBM in development
  • Understanding reasons for past failures
  • Evaluating strategies to improve the identification of more effective therapies

9:00 am Panel Discussion: GBM AGILE Goes Worldwide: Taking a Deep Dive Into How Well It Has Worked So Far & What Promise It Brings With Expansion

  • Rob Murray CBO, Global Coalition for Adaptive Research
  • Meredith Buxton CEO, Global Coalition for Adaptive Research
  • James Garner Chief Executive Officer, Kazia Therapeutics Limited
  • David Arons Chief Executive Officer, National Brain Tumor Society

Synopsis

  • Reflecting on more than 3 years of progress – lessons learned to date and plans/goals for the next 3+ years
  • Stakeholder perspectives – industry, clinical/scientific investigators, and patient advocates
  • Adaptive Global Innovative Learning Environment (AGILE): Focusing on the “LE” in AGILE

9:30 am Bizaxofusp in rGBM Patients Versus a Propensity Matched External Control Arm: Designing a Novel Phase 3 Trial with the FDA

  • Fahar Merchant President & Chief Executive Officer, Medicenna Therapeutics

Synopsis

  • Present design, mechanism, delivery and safety of bizaxofusp, an IL-4/IL-13R empowered superkine
  • Summarize Phase 2b trial comparing bizaxofusp versus a propensity matched external control arm and effect of MGMT methylation, dose, IL4R expression, and combination with bevacizumab on median survival
  • Overview of a novel Phase 3 registration trial using a Hybrid External Control Arm

10:00 am Tinostamustine: A Novel Alkylator – First Data in Glioblastoma

  • John de Groot Division Chief, Neuro- Oncology, UCSF Department of Neurosurgery

Synopsis

  • Introducing Tinostamustine as a glioblastoma therapeutic
  • Analyzing the development program and preliminary results of MDACC Phase I IIT
  • Testing tinostamustine in a Phase I GBM study in Europe

10:15 am Berubicin, An Anthracycline Analogue That Crosses the BBB, For The Treatment of GBM

Synopsis

  • Overview of the preclinical and Phase 1 clinical results of Berubicin in the treatment of GBM
  • Synopsis and preliminary results of an ongoing clinical trial comparing Berubicin to Lomustine therapy for GBM after failure of first line treatment
  • Review of safety and activity in this trial of Berubicin with the potential to establish a novel treatment strategy for GBM

10:45 am Speed Networking Break

Synopsis

This session is the ideal opportunity to introduce yourself to the attendees that

you would like to have more in-depth conversations with. Use this time to get

back to face-to-face interaction with many of the brightest minds working in the

glioblastoma field and establish meaningful business relationships.

11:45 am Immunization With Autologous Dendritic Cells is Associated With Extended Survival in Glioblastoma Patients

  • Marnix Bosch Chief Technical Officer, Northwest Biotherapeutics

Synopsis

  • Results of Phase III trial
  • Novel trial design using external controls
  • Mechanism of action of dendritic cell-based immunotherapy
  • Manufacturing of autologous cell-based products

12:15 pm BMX-001: New Therapy Showing Increased Survival in Newly Diagnosed Glioblastoma

Synopsis

  • New drug class – redox-active metallaporphyrins – positioned to transform the efficacy of radiation and chemotherapy in oncology
  • Novel BMX-001 dual action enhances tumor killing while mitigating radiation-induced side-effects
  • Discussion of ongoing randomized, 160 patient, multi-center trial

12:45 pm Lunch Break

Synopsis

Take this chance to meet the expert speakers, connect with your peers and explore our exhibition booths.

An Update On RANO 2.0 & Outlining Novel Imaging Endpoints in Phase II & III Clinical Trials

1:45 pm Assessing Response in Gliomas (RANO 2.0)

  • Patrick Wen Director - Center For Neuro-Oncology, Dana-Farber Cancer Institute

Synopsis

  • Overview of the challenges of response assessment in gliomas
  • Current data on optimal response assessment
  • Review of RANO 2.0 for glioblastomas and other gliomas in adults

2:15 pm Delving Into Imaging Endpoint Strategies for Early & Later-stage Glioblastoma Clinical Trials

Synopsis

  • For early phase clinical trials involving a limited number of patients and/or complex tumor types, a tiered approach to recognizing, quantifying, and interpreting radiographic changes is recommended, including the use of digital “flipbooks” and a modified Levin criterion, in order to increase confidence in potential therapeutic changes
  • To increase the likelihood of success in later phase trials, we recommend evaluating the proportion of patients exhibiting a meaningful change in growth rate trajectory and progression-free survival (PFS), including calculation of pre-treatment growth rates and use of a “hyperacute” baseline within days of starting experimental therapy
  • Historic data suggests objective response rate (ORR) >25%, in combination with a sufficient duration of response (DOR), leads to a meaningful increase in overall survival and a high likelihood of success in late-stage survival studies

2:45 pm ONC201 in Recurrent H3 K27M-mutant Diffuse Midline Glioma

Synopsis

  • Overview of ONC201 discovery and early clinical development
  • Review of efficacy signal refinement for ONC201 toward H3 K27M-mutant glioma
  • Summary of ONC201 efficacy it recurrent H3 K27M-mutant diffuse midline glioma

3:15 pm Tissue Preservation for Optimized GBM TreatmentBullet Points:

  • Analiz Rodriguez Associate Professor, Dept. of Neurosurgery, Director of Neuro-Oncology, University of Arkansas Medical Sciences

Synopsis

  • Reviewing the importance of tissue preservation for neuro-oncology patients
  • Understanding the role of functional precision medicine in clinical practice
  • Discussing opportunities for advanced preclinical model development

3:30 pm Afternoon Break

Synopsis

Take this chance to meet the expert speakers, connect with your peers and explore our exhibition booths.

Dodging the Side Effects & Risks of Glioblastoma Treatment Through Non-Invasive Therapies

4:00 pm Session Reserved for Kintara Therapeutics

  • Dennis Brown Chief Scientific Officer, Kintara Therapeutics

4:30 pm Understanding the World of MR-Guided Focussed Ultrasounds- Translating This Approach Into Glioblastomas

  • John de Groot Division Chief, Neuro- Oncology, UCSF Department of Neurosurgery

Synopsis

  • Unpacking the biological principles of Magnetic Resonance-guided Focused Ultrasounds (MRgFUS) in treating tumors
  • Exploring how MRgFUS has been successful in treating other pathologies like uterine cancers
  • Evaluating how feasible and effective this would be as a treatment for glioblastomas

4:45 pm Laser Interstitial Thermal Therapy: A Novel Technique to Treat Notoriously Hard-to-Reach GBM Tumors

Synopsis

  • Discovering the principles of Laser Interstitial Thermal Therapy (LITT)
  • Spotlighting how this approach is useful for patients who are resistant to stereotactic radiosurgery or suffer from radiation necrosis
  • Gaining an insight into a clinician’s perspective of how effective LITT is in practicality

5:00 pm The impact of Tumor-Treating Fields on glioblastoma residual disease

Synopsis

  • Providing an overview of the biological and biophysical effects of Tumor-Treating Fields (TTFields)
  • Describing laboratory tools to investigate the impact of TTFields in vitro and in vivo
  • Discussing the antiproliferative effects of TTFields on tumor cells isolated from glioblastoma residual disease

5:30 pm Sonodynamic Therapy: A Promising Approach to Targeting the Treatment of High-Grade Glioma

Synopsis

  • Discussing the mechanism of action of sonodynamic therapy
  • Analyzing the use of sonodynamic in high grade glioma
  • Looking at the next steps for the use of sonodynamic therapy in high grade glioma

6:00 pm Chair’s Closing Remarks & End of Day One

6:00 pm Poster Networking Session

Synopsis

After the formal presentations have finished, the scientific Poster Session is an informal part of the conference agenda, allowing you to connect with your peers in a relaxed atmosphere.

Continue to forge new and cement existing relationships while learning about the latest developments and breakthroughs in this field.